真知不罕见
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mRNA可变剪接与罕见病系列四:诺西那生纳如何治疗SMA
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2024-03-08
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面肩肱型肌营养不良:治疗方法篇
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2023-12-22
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面肩肱型肌营养不良:发病机制篇
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2023-12-11
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面肩肱型肌营养不良:临床表现篇
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2023-11-20
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修复细胞内“能量工厂”——线粒体疾病的治疗进展
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2023-10-20
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神经纤维瘤和先天性巨痣的成因及治疗方式
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2023-09-19
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成骨不全症的概况与治疗进展
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2023-08-10
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Phenopackets:一种国际通用的罕见病表型数据包标准
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2023-06-29
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干细胞治疗:为罕见病点燃治愈的希望
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2023-06-15
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mRNA可变剪接与罕见病系列三:异常的外显子跳跃与脊髓性肌萎缩
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2023-05-31
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mRNA可变剪接与罕见病系列二:可变剪接的机制与模式
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2023-05-26
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mRNA可变剪接与罕见病系列一:中心法则与蛋白质多样性
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2023-05-18
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罕见骨病与现代医学:一场关于罕见疾病的战斗
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2023-05-10
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神经和肌肉不合拍,会导致什么罕见病?
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2023-04-28